Welcome to OrphaNews, the newsletter for the rare disease community

OrphaNews, the newsletter for the rare disease community. OrphaNews is a freely available, twice-monthly electronic newsletter presenting an overview of scientific and political news about rare diseases and orphan drugs. OrphaNews is produced by Orphanet is intended for the rare disease community. It is produced with the support of Fondation IPSEN, under the aegis of Fondation de France, and the French Muscular Dystrophy Association (AFM).

In each new issue, OrphaNews reports the latest developments in the field of rare diseases and orphan drugs, including new syndromes, new genes, basic and clinical research, national and international policy, clinical trial updates, orphan drug approvals, funding opportunities, ethical, social and legal issues, news from the patient associations, upcoming events, and new publications. OrphaNews is suited to all sectors of the rare disease and orphan drugs community.

Let us know what you think about the newsletter: our annual readers' survey is open until mid-November!

OrphaNews 2023 Readers' Survey, OrphaNews 2022 Readers' Survey & OrphaNews 2019 Readers' Survey

Disclaimer : The content of newsletter represents the views of the Editorial Board only and is his/her sole responsibility; it can not be considered to reflect the views of its funders. Its funders do not accept any responsibility for use that may be made of the information it contains.